Drugs for rare conditions

Posted by & filed under Part 02: PERSPECTIVES, Part 03: GENERAL THEMES, Websites.

J Intern Med. 2006 Jul;260(1):1-10.

A journey of hope: lessons learned from studies on rare diseases and orphan

Wastfelt M, Fadeel B, Henter JI.


This article gives interesting insights on the development of orphan drugs for rare disorders. It also contains a list of great websites.


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Philippe Campeau, MD
Resident in Medical Genetics at McGill University
OMMBID Blog Administrator

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