Conlon TJ, Walter G, Owen R, Cossette T, Erger K, Gutierrez G, Goetzman E,
Matern D, Vockley J, Flotte TR.
In this article by a group from Pittsburg, proof of principle for gene therapy of a fatty acid oxidation defect (SCAD deficiency) was provided using rAAV in a murine model.
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Philippe Campeau, MD
Resident in Medical Genetics at McGill University
OMMBID Blog Administrator