Nature Reviews Genetics 7, 261-276 (April 2006)
Focus on: Monogenic disorders
Genetic medicines: treatment strategies for hereditary disorders
Timothy P. O’Connor and Ronald G. Crystal
This great review focuses on the barriers to overcome for the effective treatment of monogenic disorders in the years to come.
For more information on the treatment of inherited disorders, please see chapter 5.Â
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Philippe Campeau, MD
Resident in Medical Genetics at McGill University
OMMBID Blog Administrator